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Exon 51 skip (GSK2402968) in ambulant boys Canada

Phase III GSK exon 51 skip ambulatory boys, recruiting.
48 week trial, Montreal, we are starting soon.

weekly injection (subcutaneous), 2 muscle biopsies, etc,etc.

Here we go!

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Permalink Reply by Andrea Cleary on July 22, 2011 at 4:52pm

Thanks Paul. I couldn't get more than this for free either. Maybe one of the doctors or researchers would be kind enough to get us the full article? If that is something that can be done, I'm sure we would all appreciate it.

Permalink Reply by Paul Cliff on July 23, 2011 at 9:31am

Another parent had a copy and emailed it to me. Either friend me in Facebook or send me a message through this community site with your email address and I'll forward it to you. Otherwise, if somebody knows how to convert a pdf to a jpg format, I could post it.
Andrea Cleary said:

Thanks Paul. I couldn't get more than this for free either. Maybe one of the doctors or researchers would be kind enough to get us the full article? If that is something that can be done, I'm sure we would all appreciate it.

A.

Permalink Reply by Andrew Kerr on July 23, 2011 at 10:15am

Paul, if you send me a copy of the PDF, I can post it somewhere online that everyone can access and download as they wish.

My email is: andrew@thekerrs.ca

Once I have it, I'll put it online and post back here with the link.

Permalink Reply by Debra Chiabai on July 24, 2011 at 10:43pm

Hi Andrea,
We are already enrolled in the GSK trial in Montreal with our son Alex. I believe he is Patient 1 for that site. He's doing fine so far and the clinic staff are very caring. He's had 5 injections so far and we are headed down on Thursday for injection 6. Best of luck to you and your son.

Debra

Permalink Reply by Anup Kalra on September 8, 2011 at 6:48am

Hi Andrea and Debra,

Would you like to share some more update on trials at tis moment?

Regards....Anup

Permalink Reply by Clare Harper on September 8, 2011 at 7:42am

thanks andrea

Permalink Reply by David Beidler on September 9, 2011 at 11:49am

Try this site for the full .pdf file: http://www.duchenne.nl/1242_artfase2pro51NEJM.pdf

Andrew Kerr said:

Paul, if you send me a copy of the PDF, I can post it somewhere online that everyone can access and download as they wish.

My email is: andrew@thekerrs.ca

Once I have it, I'll put it online and post back here with the link.

Permalink Reply by Andrea Cleary on September 9, 2011 at 1:39pm

Excellent, thanks so much David! Appreciate it. Andrea

Permalink Reply by Anup Kalra on September 19, 2011 at 1:15pm

Andrea,

Sad to hear this about that boy. Must be a tough time for them.

Good to hear that your son's injection will start on Sep. 28th. Fingers crossed and best of luck to you.

Regards...Anup

Permalink Reply by JUAN PEDRO ARBULU on September 19, 2011 at 8:03pm

Andrea the best for you and your son,prayers with all you families on this trial!

Andrea Cleary said:

One of the boys eligible for the trial will have to drop-out, as he had deteriorated too much in one month and could not finish the 6-minute walk test. I don't know his age or any other details. Let's hope it was just a fluke, like he had the flu or something, and that he is doing fine. Just another reminder that time is of the essence!!!

I am thinking of him and his parents right now, want to send them some good energyl

If all goes well with the evaluation tests so far, we will start injections Sept. 28th, drug or placebo (double blind study). Won't know until week 48 which we are getting.

Permalink Reply by Andrea Cleary on September 19, 2011 at 10:30pm

Thank you Juan,

I just hope everyone can benefit from new treatments NOW!

Peace,

Andrea

Permalink Reply by Clare Harper on September 20, 2011 at 11:19am

Angela ,thinking of you and your son,all the best with this and keep us posted,exciting but stressful for you,Clare