'CRISPR-Gold' fixes Duchenne muscular dystrophy mutation in mice without viral vector

Scientists at the University of California, Berkeley, have engineered a new way to deliver CRISPR-Cas9 gene-editing technology inside cells and have demonstrated in mice that the technology can repair the mutation that causes Duchenne muscular dystrophy, a severe muscle-wasting disease. A new study shows that a single injection of CRISPR-Gold, as the new delivery system is called, into mice with Duchenne muscular dystrophy led to an 18-times-higher correction rate and a two-fold increase in a strength and agility test compared to control groups.


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This is wonderful news!  

I assume it is far from practical usage.  But still wonderful news.

Wow - Hoping and praying and hoping and praying!!  Sending so many good vibes to those scientists...possibility and hope!!!

Thank you so much for sharing this.  This is VERY good to hear.  Hoping and praying this will be a huge help for so many of us!!!  

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