'CRISPR-Gold' fixes Duchenne muscular dystrophy mutation in mice without viral vector

Scientists at the University of California, Berkeley, have engineered a new way to deliver CRISPR-Cas9 gene-editing technology inside cells and have demonstrated in mice that the technology can repair the mutation that causes Duchenne muscular dystrophy, a severe muscle-wasting disease. A new study shows that a single injection of CRISPR-Gold, as the new delivery system is called, into mice with Duchenne muscular dystrophy led to an 18-times-higher correction rate and a two-fold increase in a strength and agility test compared to control groups.

https://www.sciencedaily.com/releases/2017/10/171003202913.htm

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Permalink Reply by Bruce Ward on October 4, 2017 at 3:07pm

This is wonderful news!  

I assume it is far from practical usage.  But still wonderful news.

Permalink Reply by Sheila Haga Ungerer on October 9, 2017 at 9:39pm

Wow - Hoping and praying and hoping and praying!!  Sending so many good vibes to those scientists...possibility and hope!!!

Permalink Reply by Sheila Haga Ungerer on October 9, 2017 at 9:43pm

Thank you so much for sharing this.  This is VERY good to hear.  Hoping and praying this will be a huge help for so many of us!!!  

Permalink Reply by Jason Darienzo on October 15, 2017 at 3:58pm

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