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Permalink Reply by Sam on July 28, 2016 at 5:19am

Hi

according to my searchs, could not find anything.

you can check the clinical trial website for updates

https://clinicaltrials.gov/ct2/results?term=DMD&pg=3

good luck 

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Permalink Reply by Sanja Kogelnik on July 28, 2016 at 11:11am

Utrophin ( SMT c 1100), exon skipping 51,45,53, cat 1004 I think in next 3-6 years. Maybe stem cell by dr. Riordan.

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Permalink Reply by Goran Vasovic on October 23, 2016 at 5:58pm

By my estimate, utrophin modulation by Summit is the most promising one.

http://www.bbc.com/news/uk-england-oxfordshire-36639101

Sanja Kogelnik said:

Utrophin ( SMT c 1100), exon skipping 51,45,53, cat 1004 I think in next 3-6 years. Maybe stem cell by dr. Riordan.

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Permalink Reply by Michael Bazant on October 31, 2016 at 3:35pm

I think this is also promising with clinical trials starting in 2017.

http://solidbio.com/content/solid-biosciences-granted-us-and-eu-orp...

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Permalink Reply by Goran Vasovic on October 31, 2016 at 5:27pm

Has it the potential to treat all patients with DMD, regardless of their underlying dystrophin gene mutation ?

Michael Bazant said:

I think this is also promising with clinical trials starting in 2017.

http://solidbio.com/content/solid-biosciences-granted-us-and-eu-orp...

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Permalink Reply by Shelly on October 31, 2016 at 7:49pm

Yes it does have the potential to treat all the boys with any gene mutation !

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Permalink Reply by Steven on November 2, 2016 at 12:26pm

Not even in phase 1 safety trials as yet.  Summit (Ezutromid) probably best near term

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