I read a lot about various drugs and methods developed and tested. Anyone know if any new drug will hit the market in the next 5 years? I mean something huge that is promising?

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Hi

according to my searchs, could not find anything.

you can check the clinical trial website for updates

https://clinicaltrials.gov/ct2/results?term=DMD&pg=3

good luck 

Utrophin ( SMT c 1100), exon skipping 51,45,53, cat 1004 I think in next 3-6 years. Maybe stem cell by dr. Riordan.

By my estimate, utrophin modulation by Summit is the most promising one.

http://www.bbc.com/news/uk-england-oxfordshire-36639101

Sanja Kogelnik said:

Utrophin ( SMT c 1100), exon skipping 51,45,53, cat 1004 I think in next 3-6 years. Maybe stem cell by dr. Riordan.

I think this is also promising with clinical trials starting in 2017.

http://solidbio.com/content/solid-biosciences-granted-us-and-eu-orp...

Has it the potential to treat all patients with DMD, regardless of their underlying dystrophin gene mutation ?

Michael Bazant said:

I think this is also promising with clinical trials starting in 2017.

http://solidbio.com/content/solid-biosciences-granted-us-and-eu-orp...

Yes it does have the potential to treat all the boys with any gene mutation !

Not even in phase 1 safety trials as yet.  Summit (Ezutromid) probably best near term

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