A CRISPR Solution to Eliminating Muscular Dystrophy

http://www.perkinelmer.com/corporate/stories/crispr-eliminating-mus...

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Permalink Reply by Shelly on December 29, 2015 at 7:24pm
Hi Sanja
I think CRISPR has the potential to become a cure of this devastating disease. It really can prove a game changer . We all must do something to support this therapy like fund raising or spread awareness .
Permalink Reply by Sanja Kogelnik on December 30, 2015 at 4:47am
I agree with you. This is a CURE!!! A scientist in my country said to me that's this will be avaiable before 10 years. It is effective,cheap and I hope safe.
Permalink Reply by Shelly on December 30, 2015 at 8:48am
I had a conversation with Dr Ronald Cohn from sick kids hospital Canada. He is pretty confident about it. Let's hope for it even before 10 years.
Permalink Reply by Sanja Kogelnik on December 30, 2015 at 11:36am
Yes,many scientist,doctors believe in power of CRISPR. It must be before 10 years....in 5 years I hope, because this technology move very quick.
It is time to end Duchenne and all genetic diseases of children, to many already died! We must do something to speed up.
Permalink Reply by Jay Griffin on January 1, 2016 at 9:58am

5-10 yrs seem sooooo long....

Permalink Reply by Sanja Kogelnik on January 1, 2016 at 11:47am
Yes it is...therefore , we should step together and support CRISPR as community.
Permalink Reply by Jay Griffin on January 1, 2016 at 12:56pm

I totally agree Sanja!  I wouldn't be surprised if clinical trials come much much sooner than the traditional timeframe.  
 
Sanja Kogelnik said:

Yes it is...therefore , we should step together and support CRISPR as community.
Permalink Reply by David on January 1, 2016 at 2:50pm
New York Times ran article on Friday about CRISPR. I sure hope it accelerates, but I'm doubtful. So many immune system issues potentially. Gene therapy of any kind will receive the utmost scrutiny from FDA. Even 10 years seems optimistic to me. Hope I'm wrong.
Permalink Reply by Shelly on January 1, 2016 at 9:31pm
What ever the time frame will be .. We will have to start at some point. One day it can end DMD. You are right David! It may take more than 10 years but our hopes can sometimes pave the way to a breakthrough!!! Hope so!!!
Permalink Reply by Shelly on January 1, 2016 at 9:35pm
Anyways! Wish you all a very happy new year with the new hopes for our innocent boys!!
Permalink Reply by Moein on February 26, 2016 at 9:48pm

Will this technology be applied to all mutations?does it have any limitations?

Permalink Reply by Shelly on February 26, 2016 at 10:42pm
As far as I know it will be first available to the duplication and then target hot spot deletions exon 45 -55. If successful will move to other deletions.

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