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Good luck and best wishes to all of you brave pioneers and your sons.
Hi Jose, etc,
We too are waiting for the trial to start in Philadelphia. It's now August 23rd and still waiting. We did get an e-mail from Teesha the other day, but she hasn't responded as to when we will get our initial screening bloodkit in the mail. We're anxiously awaiting some kind of schedule or at least more information. Have you heard anything?
Joanne
Hi Jose, etc,
We too are waiting for the trial to start in Philadelphia. It's now August 23rd and still waiting. We did get an e-mail from Teesha the other day, but she hasn't responded as to when we will get our initial screening bloodkit in the mail. We're anxiously awaiting some kind of schedule or at least more information. Have you heard anything?
Joanne
Our son is in the Phase 2B study in Philadelphia. He has been on the drug/placebo (??) for two weeks as of today. We've noticed no change. Did any one notice a physical change when their boys where in the Phase 2a study? If so, how soon was it before you noticed a difference?
Angela
Hello Angela, Daniel took PTC124 about 2 years ago for 28 days and we really did not noticed any meaninful physical changes during thosse days. AS you might know there were reports from other boys showing some improvement but our Daniel didn't show it. Keep in mind that they weren't expecting any physical improvements during that study since the purpose of it was to check for safety and those results were great. None of the 38 kids showed any strong side effects. Most importantly ALL the kids produce dystrhophyne in-vitro. We are starting next week to get his EKG test doen in preparation to go to Phili soon. We just can't wait.
God bless you ALL
The Castro Gang
Angela Ryan said:Our son is in the Phase 2B study in Philadelphia. He has been on the drug/placebo (??) for two weeks as of today. We've noticed no change. Did any one notice a physical change when their boys where in the Phase 2a study? If so, how soon was it before you noticed a difference?
Angela
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