PPMD Community

Research (1,238)

Sort by:

Discussions	Replies	Latest Activity
Rapamycin prevents age-related loss of stem cells https://www.sciencedaily.com/releases/2017/12/171207141721.htm Adult stem cells replenish dying cells and regenerate damaged tissues throug… Started by Jason Darienzo	0	Dec 8, 2017
Letter of Medical Necessity I am trying to get home health care( nursing and aide ) for my 18 year old son who can not do ANYTHING for himself Does anyone have a good… Started by Najat Azar	0	Nov 8, 2017
Drug blocks deadly muscle scarring https://www.sciencedaily.com/releases/2017/10/171024103025.htm Started by Jason Darienzo	0	Oct 24, 2017
'CRISPR-Gold' fixes Duchenne muscular dystrophy mutation in mice without viral vector Scientists at the University of California, Berkeley, have engineered a new way to deliver CRISPR-Cas9 gene-editing technology inside cells… Started by Jason Darienzo	4	Oct 15, 2017 Reply by Jason Darienzo
crispr-Dr Eric olsan Hi Yesterday I Watched a video.Dr olson told crispr. summary deletıon of exon: use to crispr and dmd convert to becker( ıts look like ex… Started by ulas demirci	1	Oct 4, 2017 Reply by Bruce Ward
crispr-Dr Eric olsan Hi Yesterday I Watched a video.Dr olson told crispr. summary deletıon of exon: use to crispr and dmd convert to becker( ıts look like ex… Started by ulas demirci	0	Oct 4, 2017
Exon 45 skipping/ exon 51 skipping, Help to make a hard decision !!.PLEASE HELP. Hi We are planning to participate in exon 45 skipping trail, for our 12 year old son. Is any one already enrolled in the exon skipping tr… Started by sulthana shaik	8	Sep 25, 2017 Reply by Kirubha Balakumar
idebenone Are You giving idebenone to your kids?does it really help?does anyone uses it instead of steroids? Started by Michele Di Iorio	1	Sep 25, 2017 Reply by Bruce Ward
Exon 17 Duplication Hi my son has duplication (Exon 17) anybody with that specific Exon 17 duplication? Started by ruben lengler	1	Sep 22, 2017 Reply by David
Ataluren Today I received a letter from California children services denying services for my son because he is in the trial Ataluren , they said he… Started by Azucena Lopez de Nava	3	Sep 18, 2017 Reply by Antonio Castro