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how get sarepeta Injection in india

Dear All i want to know how we (indian ) can get sarepeta injection exondys 51 in india what will it cost .  for how much time injection w…

Started by vijender bajaj

1 Sep 27, 2016
Reply by PPMD

Etiplersen will cost $300,000

http://www.marketwatch.com/story/at-300000-a-year-sareptas-new-drug-is-considered-a-steal-2016-09-20 Great that the FDA finallly got out o…

Started by Mike O

1 Sep 23, 2016
Reply by Andrew Kerr

The agency approves a drug after an ugly bureaucratic brawl

The Wall Street Journal / Opinion The Boys Who Beat the FDA The agency approves a drug after an ugly bureaucratic brawl.  Sept. 19, 2016 M…

Started by Jason Darienzo

0 Sep 19, 2016

Sarepta Therapeutics shares jump on news of critic’s departure from FDA

"Arguably the most oppositional team leader of the review board to the approval of Duchenne Muscular Dystrophy (DMD)-treating pipeline drug…

Started by Jason Darienzo

4 Sep 19, 2016
Reply by David

INCURABLE MUSCULAR DYSTROPHY TO HAVE A CURE SOON?

http://indiatoday.intoday.in/story/aiims-muscular-dystrophy-stem-cell-therapy/1/762104.html

Started by Sanja Kogelnik

0 Sep 18, 2016

Deflazacort

My 11 year old son with DMD has been taking prednisone for 6 years now.  We want to switch to Deflazacort.  Xavier usually takes 5mg/2xday,…

Started by Jennifer Powers

4 Sep 13, 2016
Reply by jiasusa5

Heart of Bureaucratic Darkness

Heart of Bureaucratic Darkness Why won’t the FDA make a decision on a muscular dystrophy drug? The Wall Street Journal Opinion Aug. 9, 20…

Started by Jason Darienzo

0 Aug 25, 2016

As I give my son Deflazacort?

Good night, my son now weighs 24 kilograms grateful if I can recommend what the appropriate amount of daily deflazacort I should give my so…

Started by Eddy Rivera

2 Aug 23, 2016
Reply by Eddy Rivera

Cuanto debo de dar a mi hijo de deflazacort

Good night, my son now weighs 24 kilograms, agradecere if I can recommend what the appropriate amount of daily deflazacort I should give my…

Started by Eddy Rivera

1 Aug 23, 2016
Reply by Eddy Rivera

What supplements/ vitamins combination works

Hi, my son recently got diagnosed in April, he is 5. I wanted to know what supplements or vitamins would be beneficial for him. I'm just re…

Started by Nida Zuberi

7 Jul 31, 2016
Reply by Sam

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