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Drug blocks deadly muscle scarring https://www.sciencedaily.com/releases/2017/10/171024103025.htm Started by Jason Darienzo	0	Oct 24, 2017
'CRISPR-Gold' fixes Duchenne muscular dystrophy mutation in mice without viral vector Scientists at the University of California, Berkeley, have engineered a new way to deliver CRISPR-Cas9 gene-editing technology inside cells… Started by Jason Darienzo	4	Oct 15, 2017 Reply by Jason Darienzo
crispr-Dr Eric olsan Hi Yesterday I Watched a video.Dr olson told crispr. summary deletıon of exon: use to crispr and dmd convert to becker( ıts look like ex… Started by ulas demirci	1	Oct 4, 2017 Reply by Bruce Ward
crispr-Dr Eric olsan Hi Yesterday I Watched a video.Dr olson told crispr. summary deletıon of exon: use to crispr and dmd convert to becker( ıts look like ex… Started by ulas demirci	0	Oct 4, 2017
Exon 45 skipping/ exon 51 skipping, Help to make a hard decision !!.PLEASE HELP. Hi We are planning to participate in exon 45 skipping trail, for our 12 year old son. Is any one already enrolled in the exon skipping tr… Started by sulthana shaik	8	Sep 25, 2017 Reply by Kirubha Balakumar
idebenone Are You giving idebenone to your kids?does it really help?does anyone uses it instead of steroids? Started by Michele Di Iorio	1	Sep 25, 2017 Reply by Bruce Ward
Exon 17 Duplication Hi my son has duplication (Exon 17) anybody with that specific Exon 17 duplication? Started by ruben lengler	1	Sep 22, 2017 Reply by David
Ataluren Today I received a letter from California children services denying services for my son because he is in the trial Ataluren , they said he… Started by Azucena Lopez de Nava	3	Sep 18, 2017 Reply by Antonio Castro
Exon Duplications Hi All, Clinical research is going on Deletions. Anybody has any idea on Duplication's research. Serepta Pharma working on 40-53 Deletions.… Started by Sai Chand. Gurujala	0	Sep 11, 2017
Shortened telomeres linked to dysfunction in Duchenne muscular dystrophy, researchers find Shortened telomeres linked to dysfunction in Duchenne muscular dystrophy, researchers find New method reveals abnormally shortened telomere… Started by Jason Darienzo	0	Sep 7, 2017