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Any new drugs expected next 3-5 years?

I read a lot about various drugs and methods developed and tested. Anyone know if any new drug will hit the market in the next 5 years? I m…

Started by Chris

7 Nov 2, 2016
Reply by Steven

Any treatment for Exon 46

Any treatment for Exon 46

Started by srinivas

0 Nov 1, 2016

Statins and muscels

What do you think about? http://www.musculardystrophyuk.org/app/uploads/2015/02/Statins-and-muscles-2016.pdf

Started by Sanja Kogelnik

1 Oct 17, 2016
Reply by Jason Darienzo

Stem cells not a sollution?

What do you think about this research? http://musculardystrophynews.com/2016/10/05/duchenne-tongue-on-chip-model-showss-hortcomings-of-musc

Started by Michael Bazant

4 Oct 12, 2016
Reply by Michael Bazant

Pfizer Extends Age Eligibility for Myostatin Inhibitor Trial

I haven't seen this on PPMD yet so I thought I'd share. Pfizer has extended the age range for their Myostatin Inhibitor trial.  Originally…

Started by Andrew Kerr

0 Oct 9, 2016

Sarepta and Summit license partnership

http://www.fiercebiotech.com/biotech/summit-sarepta-584m-plus-dmd-pipeline-licence-pact-europe Excellent news for the community. 

Started by Steven

0 Oct 4, 2016

how get sarepeta Injection in india

Dear All i want to know how we (indian ) can get sarepeta injection exondys 51 in india what will it cost .  for how much time injection w…

Started by vijender bajaj

1 Sep 27, 2016
Reply by PPMD

Etiplersen will cost $300,000

http://www.marketwatch.com/story/at-300000-a-year-sareptas-new-drug-is-considered-a-steal-2016-09-20 Great that the FDA finallly got out o…

Started by Mike O

1 Sep 23, 2016
Reply by Andrew Kerr

The agency approves a drug after an ugly bureaucratic brawl

The Wall Street Journal / Opinion The Boys Who Beat the FDA The agency approves a drug after an ugly bureaucratic brawl.  Sept. 19, 2016 M…

Started by Jason Darienzo

0 Sep 19, 2016

Sarepta Therapeutics shares jump on news of critic’s departure from FDA

"Arguably the most oppositional team leader of the review board to the approval of Duchenne Muscular Dystrophy (DMD)-treating pipeline drug…

Started by Jason Darienzo

4 Sep 19, 2016
Reply by David


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