Research (1,242)

Discussions Replies Latest Activity

Summit Announces PhaseOut DMD Did Not Meet Primary Endpoint

Summit Announces PhaseOut DMD Did Not Meet Primary EndpointEzutromid Development to be DiscontinuedSummit to Focus on Advancing its Pipelin…

Started by Jason Darienzo

1 Jul 11, 2018
Reply by Jason Darienzo

Steriod use at a later age?

Hello, My son just turned 14 yrs old and was diagnosed with DMD at age 3. At the time of his diagnosis both his doctor and us agreed not to…

Started by Rahel kebede

0 Jun 20, 2018


Does anyone know if Summit is planning on conducting a Phase 3 trial after the Phase 2 trial is successful and we get positive results in t…

Started by Sampreet

1 May 31, 2018
Reply by Aleksandar

Exon 52 deleted

What medication do you use. Exondys 51?

Started by Apple

0 May 26, 2018


Hi Have any of your boys experienced higher cholesterol and if so, have they been given statins or any other medication to address this? 

Started by Marks33

0 Apr 27, 2018

New CRISPR method efficiently corrects Duchenne muscular dystrophy defect in heart tissue

Scientists have developed a CRISPR gene-editing technique that can potentially correct a majority of the 3,000 mutations that cause Duchenn…

Started by Jason Darienzo

1 Feb 7, 2018
Reply by Galia Ben Ishay

low back pain

does anyone here know what should i do with my kid as he suffers from chronic low back pain. i mean is there any treatment that we should d…

Started by ahmed Sayed Abdel Gawad

1 Feb 5, 2018
Reply by Kathi Kinnett

‘muscle memory’ exists at a DNA level Are there any implications on periodic dosing of steroid for DMD? 

Started by Jason Darienzo

0 Jan 30, 2018


Anyone giving Idebenone to your kids?If so, what dose and is it having anche impact?

Started by Michele Di Iorio

0 Jan 26, 2018

Facebook DMD Groups

Five months ago I found this forum and hoped that it would be a source of information about Duchenne.  Unfortunately I found that participa…

Started by Bruce Ward

0 Jan 21, 2018


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