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Utrophin Does anyone know if Summit is planning on conducting a Phase 3 trial after the Phase 2 trial is successful and we get positive results in t… Started by Sampreet	1	May 31, 2018 Reply by Aleksandar
Exon 52 deleted What medication do you use. Exondys 51? Started by Apple	0	May 26, 2018
Cholesterol Hi Have any of your boys experienced higher cholesterol and if so, have they been given statins or any other medication to address this? Started by Marks33	0	Apr 27, 2018
New CRISPR method efficiently corrects Duchenne muscular dystrophy defect in heart tissue Scientists have developed a CRISPR gene-editing technique that can potentially correct a majority of the 3,000 mutations that cause Duchenn… Started by Jason Darienzo	1	Feb 7, 2018 Reply by Galia Ben Ishay
low back pain does anyone here know what should i do with my kid as he suffers from chronic low back pain. i mean is there any treatment that we should d… Started by ahmed Sayed Abdel Gawad	1	Feb 5, 2018 Reply by Kathi Kinnett
‘muscle memory’ exists at a DNA level https://www.sciencedaily.com/releases/2018/01/180130091144.htm Are there any implications on periodic dosing of steroid for DMD? Started by Jason Darienzo	0	Jan 30, 2018
IDEBENONE Anyone giving Idebenone to your kids?If so, what dose and is it having anche impact? Started by Michele Di Iorio	0	Jan 26, 2018
Facebook DMD Groups Five months ago I found this forum and hoped that it would be a source of information about Duchenne. Unfortunately I found that participa… Started by Bruce Ward	0	Jan 21, 2018
Tamoxifen clinical trials Good day, Does anyone knows if tamoxifen is recruiting now as I read before that the estimated enrollment date will be on September 2017,an… Started by Shady	11	Jan 21, 2018 Reply by Sandro
Tamoxifen Dear all, My 9 years old son has been taking Tamoxifen for 2 months now. He is taken care of by a wonderful team in Hadassah Hospital, Jeru… Started by Galia Ben Ishay	47	Jan 21, 2018 Reply by Sandro