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Propose research that is important to you

Adding your experiences with Duchenne or Becker to ongoing research is vital to improve care and optimize potential therapies. But our com…

Started by Holly PeayLatest Reply


Staff

If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be?

If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be? PPMD’s 2012 Co…

Started by Kathi KinnettLatest Reply

Heart Transplant update

We wanted to give a update on Josh. Joshs 3yr. Heart Transplant anniversary is March 24!!! Transplant CAN be done in DMD!!!! Josh is prepar…

Started by TammyLatest Reply

Discussions Replies Latest Activity

Letter of Medical Necessity

I am trying to get home health care( nursing and aide ) for my 18 year old son who can not do ANYTHING for himself Does anyone have a good…

Started by Najat Azar

0 Nov 8

Drug blocks deadly muscle scarring

https://www.sciencedaily.com/releases/2017/10/171024103025.htm

Started by Jason Darienzo

0 Oct 24

'CRISPR-Gold' fixes Duchenne muscular dystrophy mutation in mice without viral vector

Scientists at the University of California, Berkeley, have engineered a new way to deliver CRISPR-Cas9 gene-editing technology inside cells…

Started by Jason Darienzo

4 Oct 15
Reply by Jason Darienzo

crispr-Dr Eric olsan

Hi Yesterday I Watched a video.Dr olson told crispr. summary deletıon of exon: use to crispr and dmd convert to  becker( ıts look like ex…

Started by ulas demirci

1 Oct 4
Reply by Bruce Ward

crispr-Dr Eric olsan

Hi Yesterday I Watched a video.Dr olson told crispr. summary deletıon of exon: use to crispr and dmd convert to  becker( ıts look like ex…

Started by ulas demirci

0 Oct 4

Tamoxifen

Dear all, My 9 years old son has been taking Tamoxifen for 2 months now. He is taken care of by a wonderful team in Hadassah Hospital, Jeru…

Started by Galia Ben Ishay

45 Sep 30
Reply by Bruce Ward

Tamoxifen clinical trials

Good day, Does anyone knows if tamoxifen is recruiting now as I read before that the estimated enrollment date will be on September 2017,an…

Started by Shady

8 Sep 29
Reply by Alex

Exon 45 skipping/ exon 51 skipping, Help to make a hard decision !!.PLEASE HELP.

Hi We are planning to participate in exon 45 skipping trail, for our 12 year old son. Is any one already enrolled in the exon skipping  tr…

Started by sulthana shaik

8 Sep 25
Reply by Kirubha Balakumar

idebenone

Are You giving idebenone to your kids?does it really help?does anyone uses it instead of steroids?

Started by Michele Di Iorio

1 Sep 25
Reply by Bruce Ward

Exon 17 Duplication

Hi my son has duplication (Exon 17) anybody with that specific Exon 17 duplication?

Started by ruben lengler

1 Sep 22
Reply by David

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