Research (1,231)

Featured Discussions

Propose research that is important to you

Adding your experiences with Duchenne or Becker to ongoing research is vital to improve care and optimize potential therapies. But our com…

Started by Holly PeayLatest Reply


If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be?

If you had a chance to ask researchers, providers or industry any question at all about clinical trials, what would it be? PPMD’s 2012 Co…

Started by Kathi KinnettLatest Reply

Heart Transplant update

We wanted to give a update on Josh. Joshs 3yr. Heart Transplant anniversary is March 24!!! Transplant CAN be done in DMD!!!! Josh is prepar…

Started by TammyLatest Reply

Discussions Replies Latest Activity

Exon 52 deleted

What medication do you use. Exondys 51?

Started by Alma

0 yesterday


Does anyone know if Summit is planning on conducting a Phase 3 trial after the Phase 2 trial is successful and we get positive results in t…

Started by Sampreet

0 May 13


Hi Have any of your boys experienced higher cholesterol and if so, have they been given statins or any other medication to address this? 

Started by Marks33

0 Apr 27

New CRISPR method efficiently corrects Duchenne muscular dystrophy defect in heart tissue

Scientists have developed a CRISPR gene-editing technique that can potentially correct a majority of the 3,000 mutations that cause Duchenn…

Started by Jason Darienzo

1 Feb 7
Reply by Galia Ben Ishay

low back pain

does anyone here know what should i do with my kid as he suffers from chronic low back pain. i mean is there any treatment that we should d…

Started by ahmed Sayed Abdel Gawad

1 Feb 5
Reply by Kathi Kinnett

‘muscle memory’ exists at a DNA level Are there any implications on periodic dosing of steroid for DMD? 

Started by Jason Darienzo

0 Jan 30


Anyone giving Idebenone to your kids?If so, what dose and is it having anche impact?

Started by Michele Di Iorio

0 Jan 26

Facebook DMD Groups

Five months ago I found this forum and hoped that it would be a source of information about Duchenne.  Unfortunately I found that participa…

Started by Bruce Ward

0 Jan 21

Tamoxifen clinical trials

Good day, Does anyone knows if tamoxifen is recruiting now as I read before that the estimated enrollment date will be on September 2017,an…

Started by Shady

11 Jan 21
Reply by Sandro


Dear all, My 9 years old son has been taking Tamoxifen for 2 months now. He is taken care of by a wonderful team in Hadassah Hospital, Jeru…

Started by Galia Ben Ishay

47 Jan 21
Reply by Sandro


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