This fall, PPMD is presenting a gene therapy webinar series with companies and institutions who are developing therapies for Duchenne that are commonly referred to as gene therapy, including micro-dystrophin and CRISPR/Cas9.

The second webinar in this series took place on Wednesday, September 6 at 2 PM ET, featuring Dr. Jerry Mendell of Nationwide Children’s Hospital who discussed his upcoming gene therapy trial, including trial design, inclusion/exclusion criteria, and timelines.

Host:

• Abby Bronson, SVP Research Strategy, Parent Project Muscular Dystrophy 

Speaker:

• Jerry R. Mendell, MD, PhD, Nationwide Children’s Hospital 

Webinar Recording:

Previous Webinars in this Series:

• PART 1: Gene Therapy for Duchenne - August 2017