Note: Space is limited, so those interesting in attending and/or speaking must register with PPMD in advance.
PPMD will host a Duchenne Policy Forum on clinical trials of experiment agents on December 12, 2013 from 8:30AM until 4:30PM at the Silver Spring DoubleTree by Hilton in Silver Spring, MD.
“Optimizing Clinical Trials in Duchenne Muscular Dystrophy in the New Era of Improved Care Standards” is designed to create a draft guidance for the FDA that reflects the combined experience and wisdom of the Duchenne community. Key Duchenne-community stakeholders, including the U.S. Food and Drug Administration (FDA), Center for Drug Evaluation and Research (CDER), and review divisions, are committed to the success of this meeting.
Modeled after the successful meeting held by our sister organization United Parent Project Muscular Dystrophy in London in the spring, different expert(s) will present on four areas:
Following each presentation, comments from the Duchenne community will be welcome. Speakers are requested to focus comments on the following:
Comments will be limited to three minutes. Our aim is to hear from all who have interest in the area as time allows. Upon arriving at the conference, there will be a sign up available for all those interested in speaking.
For those who are unable to attend, you can submit your story online (even if you wish to attend you can still submit a story). PPMD has been compiling stories for months, ensuring that the patient voice is heard, and sharing them with the FDA.
Silver Spring DoubleTree by Hilton
8727 Colesville Road
Silver Spring, MD 20910
PPMD does not have a reserved room block or discounted rate for this event. View a list of area hotels.