As a mother who lost two sons to this dreadful disease, I am driven to find every way possible to help bring new therapies to families, to end Duchenne. PPMD supports and agrees with all parents urging the agency to accept Sarepta’s submission for the approval of eteplirsen, as well as any other therapy that shows similar promise. The voices of patients and caregivers are critical to the process of drug development and we believe the message is being heard.
PPMD is doing everything it can to enable the FDA to speed the approval of new therapies to all who so desperately need them. We continue to demand that the FDA use all available tools given to them by Congress to approve rapidly treatments that show safety and effectiveness. Here are 3 simple actions you can take to help.
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UPDATE: 88 #MDCAREAct cosponsors in the House, 21 in the Senate! Let's get to 100 & 25 — We can do it! Tell your members of Congress to take action to #EndDuchenne: www.ParentProjectMD.org/TakeAction And help us thank our newest cosponsors: Congressman Stephen Fincher [TN-8], Congressman Frank Wolf [VA-10], & Congressman Steve Daines [MT-At Large]
A great article from The Huffington Post on Team Joseph's fight to #endDuchenne. Thank you Northwestern University Dance Marathon for providing the Duchenne community with such an amazing opportunity, and good luck to all 1,500 dancers tomorrow!