PPMD Community

Photos

  • Add Photos
  • View All

News from PPMD

Loading… Loading feed

 

Welcome to the PPMD Community.

Getting started is easy. Just click one of the icons below.


Read News

Join Groups

View Discussions

Build Resources

Attend Events

Latest Activity

Profile IconMegan Reading, Feriel Khadri and Wendy Chouteau joined PPMD Community
yesterday
Praveen favorited Brooke Lyons's profile
yesterday

Staff
PPMD posted a blog post

Capricor Announces New Pre-Clinical Study Finds Repeat Doses of CAP-1002 Lead to Enhanced Exercise Capacity in Duchenne Muscular Dystrophy Disease Model

Capricor Therapeutics has announced that researchers found that repeat dosing of the company’s proprietary cellular therapy, CAP-1002, yields an increase in exercise performance in a disease model of Duchenne muscular dystrophy, the mdx mouse. The upcoming HOPE-2 clinical trial will test the safety and efficacy of repeat doses of CAP-1002 in boys and young men with Duchenne. …See More
Friday
Praveen joined Roxanne's group
Thumbnail

Outliers - Intermediate between Duchenne & Becker MD

The reading frame rule holds true 90% of the time. There remains those 10% that does not fit dmd/bmd phenotype. There is a 3rd form that may be considered as an intermediate between Duchenne and Becker MD(mild DMD or severe BMD.See More
Friday

Staff
Kathi Kinnett posted a blog post

PPMD & NIH to Host “Contractures in Duchenne and Other Neuromuscular Conditions”

 PPMD and NIH are convening a group of more than 60 researchers, post-docs, neurologists, surgeons, industry partners, physiatrists, and physical therapists on April 19-20, 2018, who have experience and expertise in the development, prevention, and management of contractures to discuss these critical issues. We just don’t know…See More
Thursday
Profile IconMarco Vinicio Porras Suarez and Tammy McGuire joined PPMD Community
Apr 18

Staff
PPMD posted a blog post

Solid Biosciences Provides Update On SGT-001 Clinical Development Program For Duchenne

Solid has provided a letter to the community with the latest news on their halted IGNITE DMD program due to a serious adverse event experienced by the first patient dosed with SGT-001. While the patient continues to do well, Solid has been able to successfully resolve the previously-announced partial clinical hold on the planned high dose of SGT-001 in IGNITE DMD, which was due to manufacturing-related questions from the FDA. While encouraging, IGNITE DMD remains on hold until they address the…See More
Apr 18

Staff
PPMD posted a blog post

Pfizer Doses First Patient Using Investigational Mini-Dystrophin Gene Therapy for the Treatment of Duchenne Muscular Dystrophy

PPMD is thrilled to learn that Pfizer Inc. has initiated a Phase 1b clinical trial for its mini-dystrophin gene therapy candidate, PF-06939926, in Duchenne, with the first boy receiving an infusion of the mini-dystrophin gene on March 22, administered under the supervision of principal investigator, Edward Smith, MD, Associate Professor of Pediatrics and Neurology at Duke University Medical Center. Screening and enrollment of patients is expected to continue at up to four clinical research…See More
Apr 16

Staff
Ryan Fischer posted a blog post

70 Members of Congress Send Letter of Strong Support for Duchenne Priorities for Next Year’s Budget

We are pleased to report our final numbers for the FY19 letters. In total, 19 Senators signed onto the Senate FY19 letter, joining 51 members of the House. That makes a solid 70 members of Congress (House and Senate combined) sending a strong message of support behind Duchenne research, public health, drug development, and patient support initiatives. They provide strategic direction for the federal agencies that touch Duchenne. Given the tremendous level of uncertainty at the federal level…See More
Apr 16
Avinash Dewani is now a member of PPMD Community
Apr 16

Staff
PPMD posted a blog post

Roche Restarts RG62026 Phase 2/3 Study

Roche has provided an update to the community announcing that they have restarted recruitment of RG6206, an investigational anti-myostatin adnectin, in ambulatory boys with Duchenne. PPMD will be hosting a webinar with Roche in the coming weeks and we look forward to learning more.Read the update from Roche:  11 April 2018 Dear…See More
Apr 11
Jack dayon is now a member of PPMD Community
Apr 11

Staff
Kathi Kinnett posted a blog post

Why is Bone Health Important?

Just like a house needs a stable frame, your body needs a stable skeleton. Bone health is important for anyone living with Duchenne, whether walking (ambulatory) or those no longer able to walk without the assistance of a wheelchair or scooter (non-ambulatory). People of all ages living with Duchenne have weak bones, especially if…See More
Apr 11
Praveen joined Eileen DeLong's group
Thumbnail

Exon Deletion 3-7

Connect with other families with exon deletion 3-7.
Apr 10
Profile IconCindy Collins and Praveen joined PPMD Community
Apr 10
Robin Taylor replied to ven's discussion Brenda Wong Leaving CMC
"Shawn - thanks for the update on Dr. Wong. Worcester, Massachusetts is gaining a great doctor --- wish she was coming to Nebraska."
Mar 30
 
 
 

Need help using this community site? Visit Ning's Help Page.

Members

Events

© 2018   Created by PPMD.   Powered by

Badges  |  Report an Issue  |  Privacy Policy  |  Terms of Service